The following articles identify new advancements and promising
research regarding Niemann-Pick disease.
Clinical Trial of Cyclodextrin being Planned by NIH
The National Institutes of Health (NIH) is planning a clinical trial of cyclodextrin for use in patients with Niemann-Pick Disease Type C (NPC). For more information about this exciting research, visit the National Niemann-Pick Disease Foundation's cyclodextrin page at www.nnpdf.org/Cyclodextrin.html
NPC Clinical Trial Opportunity
Message from Dr. Forbes "Denny" Porter, National Institutes of Health. The NNPDF has received an update from Dr. Denny Porter at the National Institutes of Health regarding an upcoming NPC Clinical Trial opportunity. Please click here to read Dr. Porter's message.
Researchers at the Washington University School of Medicine in St. Louis propose a new treatment approach for Niemann-Pick Disease http://mednews.wustl.edu/news/page/normal/10988.html
Year-1 results show that miglustat improves or stabilizes several clinically relevant markers of Niemann-Pick Type C http://www.medicalnewstoday.com/articles/80377.php
Evaluation of Biochemical Markers and Clinical Investigation of Niemann-Pick Disease, Type C http://clinicaltrials.gov/ct/show/NCT00344331?order=1